{"id":507,"date":"2026-05-05T13:57:37","date_gmt":"2026-05-05T04:57:37","guid":{"rendered":"https:\/\/rmnw.jp\/teams\/?p=507"},"modified":"2026-05-05T13:57:38","modified_gmt":"2026-05-05T04:57:38","slug":"rm10-%e7%ac%ac%e5%8d%81%e7%ab%a0-%e7%9c%bc%e7%a7%91","status":"publish","type":"post","link":"https:\/\/rmnw.jp\/teams\/?p=507","title":{"rendered":"RM10.\u7b2c\u5341\u7ae0 \u773c\u79d1"},"content":{"rendered":"\n<figure class=\"wp-block-embed is-type-video is-provider-youtube wp-block-embed-youtube wp-embed-aspect-16-9 wp-has-aspect-ratio\"><div class=\"wp-block-embed__wrapper\">\n<iframe loading=\"lazy\" title=\"RM10.\u7b2c\u5341\u7ae0 \u773c\u79d1\" width=\"500\" height=\"281\" src=\"https:\/\/www.youtube.com\/embed\/CkTYW8Hi4RE?feature=oembed\" frameborder=\"0\" allow=\"accelerometer; autoplay; clipboard-write; encrypted-media; gyroscope; picture-in-picture; web-share\" referrerpolicy=\"strict-origin-when-cross-origin\" allowfullscreen><\/iframe>\n<\/div><\/figure>\n\n\n\n\t\t<div class=\"wppdfemb-frame-container-1\" style=\"-webkit-overflow-scrolling:auto;\">\n\t\t\t<iframe class=\"pdfembed-iframe nonfullscreen wppdf-emb-iframe-1\"\n\t\t\t\tsrc=\"https:\/\/rmnw.jp\/teams\/?pdfemb-data=eyJwZGZJRCI6NTA4LCJ1cmwiOiJodHRwczpcL1wvcm1udy5qcFwvdGVhbXNcL3dwLWNvbnRlbnRcL3VwbG9hZHNcLzIwMjZcLzA1XC9STTEwLlx1N2IyY1x1NTM0MVx1N2FlMC1cdTc3M2NcdTc5ZDEucGRmIiwiaW5kZXgiOjF9\"\n\t\t\t\t\t\t\t\tdata-pdf-id=\"508\"\n\t\t\t\tdata-pdf-index=\"1\"\n\t\t\t\tstyle=\"border:none;width:100%;max-width:100%;height:100vh;\"\n\t\t\t\tscrolling=\"yes\">\n\t\t\t<\/iframe>\n\t\t<\/div>\n\n\t\t\n\n\n<h1 class=\"wp-block-heading\">\u773c\u79d1\u9818\u57df\u306b\u304a\u3051\u308b\u518d\u751f\u533b\u7642\u3068\u907a\u4f1d\u5b50\u6cbb\u7642\uff1a\u6700\u65b0\u52d5\u5411\u3068\u81e8\u5e8a\u7684\u8003\u5bdf<\/h1>\n\n\n\n<h2 class=\"wp-block-heading\">\u30a8\u30b0\u30bc\u30af\u30c6\u30a3\u30d6\u30fb\u30b5\u30de\u30ea\u30fc<\/h2>\n\n\n\n<p>\u773c\u79d1\u9818\u57df\u306f\u3001\u518d\u751f\u533b\u7642\u304a\u3088\u3073\u907a\u4f1d\u5b50\u6cbb\u7642\u306e\u793e\u4f1a\u5b9f\u88c5\u306b\u304a\u3044\u3066\u4e16\u754c\u3092\u30ea\u30fc\u30c9\u3059\u308b\u5206\u91ce\u3067\u3042\u308b\u3002\u773c\u7403\u306f\u300c\u514d\u75ab\u7279\u6a29\uff08Immune Privilege\uff09\u300d\u3092\u6709\u3057\u3001\u8840\u6db2\u7db2\u819c\u95a2\u9580\uff08BRB\uff09\u306b\u3088\u3063\u3066\u4fdd\u8b77\u3055\u308c\u3066\u3044\u308b\u305f\u3081\u3001\u7d30\u80de\u79fb\u690d\u3084\u907a\u4f1d\u5b50\u5c0e\u5165\u306e\u6a19\u7684\u3068\u3057\u3066\u6975\u3081\u3066\u9069\u3057\u3066\u3044\u308b\u3002\u73fe\u5728\u3001\u30d2\u30c8\u591a\u80fd\u6027\u5e79\u7d30\u80de\uff08hPSC\uff09\u3092\u7528\u3044\u305f\u773c\u79d1\u95a2\u9023\u30d7\u30ed\u30b0\u30e9\u30e0\u306f\u4e16\u754c21\u30ab\u56fd\u3067\u5c55\u958b\u3055\u308c\u3066\u304a\u308a\u3001115\u306e\u30d7\u30ed\u30b0\u30e9\u30e0\u300183\u306e\u81e8\u5e8a\u8a66\u9a13\u304c\u9032\u884c\u4e2d\u3067\u3042\u308b\u3002<\/p>\n\n\n\n<p>\u4e3b\u306a\u9032\u5c55\u3068\u3057\u3066\u3001\u52a0\u9f62\u9ec4\u6591\u5909\u6027\uff08AMD\uff09\u306b\u5bfe\u3059\u308biPS\u7d30\u80de\u7531\u6765\u7db2\u819c\u8272\u7d20\u4e0a\u76ae\uff08RPE\uff09\u7d30\u80de\u79fb\u690d\u3001\u89d2\u819c\u75be\u60a3\u306b\u5bfe\u3059\u308b\u57f9\u990a\u89d2\u819c\u4e0a\u76ae\u30b7\u30fc\u30c8\uff08Nepic\u7b49\uff09\u3084iPS\u7d30\u80de\u7531\u6765\u89d2\u819c\u4e0a\u76ae\u7d30\u80de\u30b7\u30fc\u30c8\uff08iCEPS\uff09\u3001\u3055\u3089\u306b\u7db2\u819c\u8272\u7d20\u5909\u6027\uff08RP\uff09\u306b\u5bfe\u3059\u308b\u907a\u4f1d\u5b50\u6cbb\u7642\u85ac\u300c\u30eb\u30af\u30b9\u30bf\u30fc\u30ca\u300d\u306e\u5b9f\u7528\u5316\u304c\u6319\u3052\u3089\u308c\u308b\u3002\u7279\u306b\u30eb\u30af\u30b9\u30bf\u30fc\u30ca\u306f\u3001\u672c\u90a6\u3067\u306e\u85ac\u4fa1\u304c\u4e21\u773c\u3067\u7d049,920\u4e07\u5186\u306b\u9054\u3059\u308b\u306a\u3069\u3001\u9ad8\u984d\u7642\u990a\u8cbb\u67a0\u7d44\u307f\u306e\u8ad6\u70b9\u3068\u3082\u306a\u3063\u3066\u3044\u308b\u3002\u4eca\u5f8c\u306e\u8ab2\u984c\u306f\u3001\u79fb\u690d\u7d30\u80de\u306e\u9577\u671f\u751f\u7740\u3001\u8108\u7d61\u7db2\u819c\u840e\u7e2e\uff08CRA\uff09\u306a\u3069\u306e\u5408\u4f75\u75c7\u7ba1\u7406\u3001\u304a\u3088\u3073\u6301\u7d9a\u7684\u306a\u6297VEGF\u52b9\u679c\u3092\u7dad\u6301\u3059\u308b\u6b21\u4e16\u4ee3\u907a\u4f1d\u5b50\u6cbb\u7642\u306e\u958b\u767a\u3067\u3042\u308b\u3002<\/p>\n\n\n\n<p>&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8211;<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">1. \u773c\u7403\u306e\u69cb\u9020\u7684\u7279\u6027\u3068\u6cbb\u7642\u306e\u57fa\u76e4<\/h2>\n\n\n\n<h3 class=\"wp-block-heading\">1.1 \u7db2\u819c\u306e\u5c64\u69cb\u9020<\/h3>\n\n\n\n<p>\u7db2\u819c\u306f\u3001\u5149\u3092\u53d7\u5bb9\u3057\u96fb\u6c17\u4fe1\u53f7\u306b\u5909\u63db\u3059\u308b\u8907\u96d1\u306a\u591a\u5c64\u69cb\u9020\u3092\u6709\u3057\u3066\u3044\u308b\u3002<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u4e3b\u8981\u306a\u5c64:<\/strong> \u5185\u5883\u754c\u819c\u3001\u795e\u7d4c\u7dda\u7dad\u5c64\u3001\u795e\u7d4c\u7bc0\u7d30\u80de\u5c64\u3001\u5185\u5883\u754c\u7db2\u3001\u5185\u9846\u7c92\u5c64\u3001\u5916\u5883\u754c\u7db2\u3001\u5916\u9846\u7c92\u5c64\u3001\u8996\u7d30\u80de\u5c64\u3001\u7db2\u819c\u8272\u7d20\u4e0a\u76ae\uff08RPE\uff09\u3001\u8108\u7d61\u819c\u3002<\/li>\n\n\n\n<li><strong>\u6a19\u7684\u90e8\u4f4d:<\/strong> \u73fe\u5728\u306e\u518d\u751f\u533b\u7642\u306e\u591a\u304f\u306f\u3001\u8996\u529b\u7dad\u6301\u306b\u4e0d\u53ef\u6b20\u306aRPE\u5c64\u304a\u3088\u3073\u8996\u7d30\u80de\u5c64\u3092\u6a19\u7684\u3068\u3057\u3066\u3044\u308b\u3002<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\">1.2 \u514d\u75ab\u7279\u6a29\uff08Immune Privilege\uff09<\/h3>\n\n\n\n<p>\u773c\u7403\u304c\u518d\u751f\u533b\u7642\u306b\u9069\u3057\u3066\u3044\u308b\u6700\u5927\u306e\u7406\u7531\u306f\u3001\u72ec\u81ea\u306e\u514d\u75ab\u6291\u5236\u74b0\u5883\u306b\u3042\u308b\u3002<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u9632\u5fa1\u6a5f\u69cb:<\/strong> \u8840\u6db2\u7db2\u819c\u95a2\u9580\uff08BRB\uff09\u306e\u5b58\u5728\u306b\u52a0\u3048\u3001\u524d\u623f\u95a2\u9023\u514d\u75ab\u504f\u5411\uff08ACAID\uff09\u3084TGF-\u03b2\u306a\u3069\u306e\u6291\u5236\u56e0\u5b50\u306b\u3088\u308a\u3001\u79fb\u690d\u7d30\u80de\u306b\u5bfe\u3059\u308b\u62d2\u7d76\u53cd\u5fdc\u304c\u6291\u5236\u3055\u308c\u308b\u3002<\/li>\n\n\n\n<li><strong>\u81e8\u5e8a\u7684\u610f\u7fa9:<\/strong> \u3053\u308c\u306b\u3088\u308a\u3001\u4ed6\u5bb6\u7d30\u80de\u79fb\u690d\uff08\u4f8b\uff1aHLA\u9069\u5408iPS\u7d30\u80de\uff09\u306e\u6210\u529f\u7387\u304c\u9ad8\u307e\u308b\u3002<\/li>\n<\/ul>\n\n\n\n<p>&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8211;<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">2. \u52a0\u9f62\u9ec4\u6591\u5909\u6027\uff08AMD\uff09\u306e\u518d\u751f\u533b\u7642\u30fb\u907a\u4f1d\u5b50\u6cbb\u7642<\/h2>\n\n\n\n<p>AMD\u306f\u3001\u9ad8\u9f62\u8005\u306e\u5931\u660e\u306e\u4e3b\u8981\u539f\u56e0\u3067\u3042\u308a\u3001RPE\u7d30\u80de\u306e\u5909\u6027\u304c\u75c5\u614b\u306e\u4e2d\u5fc3\u3067\u3042\u308b\u3002<\/p>\n\n\n\n<h3 class=\"wp-block-heading\">2.1 \u7d30\u80de\u79fb\u690d\u6cbb\u7642\u306e\u81e8\u5e8a\u5b9f\u7e3e<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>RIKEN\u306b\u3088\u308b\u4e16\u754c\u521d\u306e\u81e8\u5e8a\u8a66\u9a13 (2014\u5e74):<\/strong> \u81ea\u5bb6iPS\u7d30\u80de\u7531\u6765RPE\u30b7\u30fc\u30c8\u3092\u6ef2\u51fa\u578bAMD\u60a3\u8005\u306b\u79fb\u690d\u30022\u5e74\u9593\u306e\u89b3\u5bdf\u3067\u751f\u7740\u3068\u5b89\u5168\u6027\u304c\u78ba\u8a8d\u3055\u308c\u305f\uff08Mandai et al. NEJM 2017\uff09\u3002<\/li>\n\n\n\n<li><strong>HLA\u9069\u5408\u4ed6\u5bb6iPS\u7d30\u80de\u79fb\u690d (2017\u5e74):<\/strong> CiRA\u306eHLA\u30b9\u30c8\u30c3\u30af\u3092\u7528\u3044\u305f\u4ed6\u5bb6iPS-RPE\u61f8\u6fc1\u6db2\u79fb\u690d\u30025\u4f8b\u4e2d4\u4f8b\u3067\u5b89\u5168\u6027\u3068\u4e00\u5b9a\u306e\u8996\u529b\u7dad\u6301\u3092\u78ba\u8a8d\uff08Sugita et al. J Clin Med 2020\uff09\u3002<\/li>\n\n\n\n<li><strong>\u6d77\u5916\u306e\u52d5\u5411:<\/strong>\n<ul class=\"wp-block-list\">\n<li><strong>OpRegen (Lineage\/Roche):<\/strong> ESC\u7531\u6765RPE\u7d30\u80de\u79fb\u690d\u3002\u5730\u56f3\u72b6\u840e\u7e2e\uff08GA\uff09\u60a3\u8005\u306b\u304a\u3044\u3066\u3001ETDRS\u8996\u529b\u8868\u3067\u6709\u610f\u306a\u6539\u5584\uff08+7.7\u6587\u5b57\/12\u30f6\u6708\uff09\u3092\u5831\u544a\u3002<\/li>\n\n\n\n<li><strong>CPCB-RPE1:<\/strong> \u30d1\u30ea\u30ec\u30f3\u819c\u3092\u7528\u3044\u305fhESC-RPE\u30b7\u30fc\u30c8\u3002GA\u60a3\u800516\u4f8b\u4e2d27%\u3067+5\u6587\u5b57\u4ee5\u4e0a\u306e\u6539\u5584\u3002<\/li>\n<\/ul>\n<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\">2.2 \u6b21\u4e16\u4ee3\u907a\u4f1d\u5b50\u6cbb\u7642\uff08\u6297VEGF\u6cbb\u7642\u306e\u6301\u7d9a\u5316\uff09<\/h3>\n\n\n\n<p>\u73fe\u5728\u3001\u983b\u56de\u306a\u785d\u5b50\u4f53\u5185\u6ce8\u5c04\u3092\u5fc5\u8981\u3068\u3059\u308b\u6297VEGF\u7642\u6cd5\u3092\u3001\u4e00\u5ea6\u306e\u6295\u4e0e\u3067\u9577\u671f\u6301\u7d9a\u3055\u305b\u308b\u907a\u4f1d\u5b50\u6cbb\u7642\u306e\u958b\u767a\u304c\u52a0\u901f\u3057\u3066\u3044\u308b\u3002<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>ABBV-RGX-314:<\/strong> AAV8\u30d9\u30af\u30bf\u30fc\u3092\u7528\u3044\u3001\u30e9\u30cb\u30d3\u30ba\u30de\u30d6\u76f8\u5f53\u306eFab\u65ad\u7247\u3092\u767a\u73fe\u3002<\/li>\n\n\n\n<li><strong>4D-150:<\/strong> R100\u30d9\u30af\u30bf\u30fc\u3092\u7528\u3044\u3001\u30a2\u30d5\u30ea\u30d9\u30eb\u30bb\u30d7\u30c8\u3068VEGF-C miRNA\u3092\u767a\u73fe\u3002PRISM\u8a66\u9a13\uff08Phase 2\uff09\u306b\u304a\u3044\u3066\u3001\u6ce8\u5c04\u983b\u5ea6\u309283\u301c89%\u524a\u6e1b\u3059\u308b\u3053\u3068\u306b\u6210\u529f\u3002<\/li>\n<\/ul>\n\n\n\n<p>&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8211;<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">3. \u89d2\u819c\u75be\u60a3\u306e\u518d\u751f\u533b\u7642<\/h2>\n\n\n\n<p>\u89d2\u819c\u9818\u57df\u3067\u306f\u3001\u8f2a\u90e8\u5e79\u7d30\u80de\u6b20\u640d\u75c7\uff08LSCD\uff09\u3084\u6c34\u75b1\u6027\u89d2\u819c\u75c7\u3092\u5bfe\u8c61\u3068\u3057\u305f\u88fd\u54c1\u304c\u3059\u3067\u306b\u5b9f\u7528\u5316\u30d5\u30a7\u30fc\u30ba\u306b\u3042\u308b\u3002<\/p>\n\n\n\n<h3 class=\"wp-block-heading\">3.1 LSCD\uff08\u8f2a\u90e8\u5e79\u7d30\u80de\u6b20\u640d\u75c7\uff09\u6cbb\u7642<\/h3>\n\n\n\n<figure class=\"wp-block-table\"><table class=\"has-fixed-layout\"><tbody><tr><td>\u88fd\u54c1\u30fb\u30d7\u30ed\u30b0\u30e9\u30e0\u540d<\/td><td>\u7531\u6765\u7d30\u80de<\/td><td>\u30b9\u30c6\u30fc\u30bf\u30b9\u30fb\u7279\u5fb4<\/td><\/tr><tr><td><strong>Nepic (J-TEC)<\/strong><\/td><td>\u81ea\u5bb6\u57f9\u990a\u89d2\u819c\u4e0a\u76ae<\/td><td>2020\u5e74\u627f\u8a8d\u3002SJS\u7b49\u306eLSCD\u60a3\u8005\u3092\u5bfe\u8c61\u3002<\/td><\/tr><tr><td><strong>COMET<\/strong><\/td><td>\u81ea\u5bb6\u57f9\u990a\u53e3\u8154\u7c98\u819c\u4e0a\u76ae<\/td><td>2021\u5e74\u627f\u8a8d\u3002LSCD\u60a3\u8005\u3092\u5bfe\u8c61\u3002<\/td><\/tr><tr><td><strong>iCEPS (\u5927\u962a\u5927\u5b66)<\/strong><\/td><td>iPS\u7d30\u80de\u7531\u6765\u89d2\u819c\u4e0a\u76ae<\/td><td>FIH\u8a66\u9a13\uff084\u4f8b\uff09\u3067BCVA\u306e\u6539\u5584\uff08\u4f8b\uff1a0.15\u21920.7\uff09\u3092\u78ba\u8a8d\u30022026\u5e74\u9803\u306e\u627f\u8a8d\u3092\u76ee\u6307\u3059\u3002<\/td><\/tr><tr><td><strong>Holoclar<\/strong><\/td><td>\u81ea\u5bb6\u57f9\u990a\u89d2\u819c\u4e0a\u76ae<\/td><td>EU\u3067\u521d\u306eATMP\uff08\u518d\u751f\u533b\u7642\u7b49\u88fd\u54c1\uff09\u3068\u3057\u3066\u627f\u8a8d\uff082015\u5e74\uff09\u3002<\/td><\/tr><\/tbody><\/table><\/figure>\n\n\n\n<h3 class=\"wp-block-heading\">3.2 \u6c34\u75b1\u6027\u89d2\u819c\u75c7\uff08\u89d2\u819c\u5185\u76ae\uff09\u6cbb\u7642<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>AURN001 (Aurion Biotech):<\/strong> \u57f9\u990a\u89d2\u819c\u5185\u76ae\u7d30\u80de\u3068ROCK\u963b\u5bb3\u5264\uff08Y-27632\uff09\u306e\u524d\u623f\u5185\u6ce8\u5165\u7642\u6cd5\u3002<\/li>\n\n\n\n<li><strong>\u81e8\u5e8a\u5b9f\u7e3e:<\/strong> Kinoshita\u3089\uff08NEJM 2018\uff09\u306e\u5831\u544a\u3067\u306f\u3001\u79fb\u690d\u5f8c\u306e\u7d30\u80de\u5bc6\u5ea6\u304c2,500 cells\/mm\u00b2\u3092\u8d85\u3048\u3001\u826f\u597d\u306a\u8996\u529b\u6539\u5584\u3068\u5b89\u5168\u6027\u304c\u793a\u3055\u308c\u305f\u3002\u672c\u90a6\u3067\u306f2024\u5e749\u6708\u306b\u300c\u30bb\u30eb\u30ea\u30a2\u30f3\u30fb\u30a2\u30a4\u30fb\u30bb\u30eb\u306e\u540d\u79f0\u3067\u627f\u8a8d\u3002<\/li>\n<\/ul>\n\n\n\n<p>&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8211;<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">4. \u7db2\u819c\u8272\u7d20\u5909\u6027\uff08RP\uff09\u3068\u907a\u4f1d\u5b50\u6cbb\u7642<\/h2>\n\n\n\n<p>\u7db2\u819c\u8272\u7d20\u5909\u6027\u306f\u907a\u4f1d\u5b50\u5909\u7570\u306b\u8d77\u56e0\u3059\u308b\u75be\u60a3\u7fa4\u3067\u3042\u308a\u3001\u7279\u5b9a\u306e\u907a\u4f1d\u5b50\u3092\u6a19\u7684\u3068\u3057\u305f\u6cbb\u7642\u304c\u9032\u3093\u3067\u3044\u308b\u3002<\/p>\n\n\n\n<h3 class=\"wp-block-heading\">4.1 \u30eb\u30af\u30b9\u30bf\u30fc\u30ca\uff08Luxturna\uff09<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>\u6a19\u7684\u907a\u4f1d\u5b50:<\/strong> RPE65\uff08\u4e21\u30a2\u30ec\u30eb\u6027\u5909\u7570\uff09\u3002<\/li>\n\n\n\n<li><strong>\u52b9\u679c:<\/strong> MLMT\uff08\u591a\u8f1d\u5ea6\u79fb\u52d5\u30c6\u30b9\u30c8\uff09\u306b\u304a\u3044\u3066\u3001\u6709\u610f\u306a\u8996\u6a5f\u80fd\u6539\u5584\uff08+1.6\u70b9\uff09\u3092\u8a3c\u660e\u3002<\/li>\n\n\n\n<li><strong>\u4fa1\u683c:<\/strong> \u4e21\u773c\u5206\u30679,920\u4e07\u5186\uff08\u65e5\u672c\u85ac\u4fa1\u30012023\u5e748\u6708\u6642\u70b9\uff09\u3002\u7c73\u56fd\u306e\u7d0485\u4e07\u30c9\u30eb\u306b\u5bfe\u3057\u3001\u672c\u90a6\u306f\u7d04\u534a\u984d\u306e\u6c34\u6e96\u3002<\/li>\n\n\n\n<li><strong>\u8ab2\u984c:<\/strong> \u8108\u7d61\u7db2\u819c\u840e\u7e2e\uff08CRA\uff09\u304c13\u301c50%\u306e\u983b\u5ea6\u3067\u767a\u751f\u3002\u307e\u305f\u3001\u4e2d\u5fc3\u7aa9\u840e\u7e2e\u4f8b\u3067\u306f\u52b9\u679c\u304c\u9650\u5b9a\u7684\u3002<\/li>\n<\/ul>\n\n\n\n<h3 class=\"wp-block-heading\">4.2 \u958b\u767a\u4e2d\u306e\u65b0\u85ac<\/h3>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>AGTC-501 \/ bota-vec:<\/strong> RPGR\u907a\u4f1d\u5b50\u3092\u6a19\u7684\u3068\u3057\u305fXLRP\uff08X\u9023\u9396\u6027\u7db2\u819c\u8272\u7d20\u5909\u6027\uff09\u6cbb\u7642\u85ac\u3002Phase 3\u8a66\u9a13\u304c\u9032\u884c\u4e2d\u3002<\/li>\n\n\n\n<li><strong>MCO-010:<\/strong> \u5149\u907a\u4f1d\u5b66\uff08Optogenetics\uff09\u3092\u7528\u3044\u305f\u6cbb\u7642\u3002BLA\uff08\u65b0\u85ac\u627f\u8a8d\u7533\u8acb\uff09\u5be9\u67fb\u4e2d\u3002<\/li>\n<\/ul>\n\n\n\n<p>&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8211;<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">5. \u7cd6\u5c3f\u75c5\u7db2\u819c\u75c7\uff08DR\uff09\u3078\u306e\u5fdc\u7528<\/h2>\n\n\n\n<p>\u7cd6\u5c3f\u75c5\u7db2\u819c\u75c7\u306b\u304a\u3044\u3066\u3082\u3001\u6297VEGF\u907a\u4f1d\u5b50\u6cbb\u7642\u306b\u3088\u308b\u9577\u671f\u6291\u5236\u304c\u671f\u5f85\u3055\u308c\u3066\u3044\u308b\u3002<\/p>\n\n\n\n<ul class=\"wp-block-list\">\n<li><strong>ABBV-RGX-314 (ALTITUDE\u8a66\u9a13):<\/strong> 2\u6bb5\u968e\u306eDRSS\uff08\u7cd6\u5c3f\u75c5\u7db2\u819c\u75c7\u91cd\u75c7\u5ea6\u30b9\u30b1\u30fc\u30eb\uff09\u6539\u5584\u304c70.8%\u306e\u75c7\u4f8b\u3067\u898b\u3089\u308c\u305f\u3002<\/li>\n\n\n\n<li><strong>4D-150 (SPECTRA\u8a66\u9a13):<\/strong> \u7cd6\u5c3f\u75c5\u9ec4\u6591\u6d6e\u816b\uff08DME\uff09\u60a3\u8005\u306b\u304a\u3044\u3066\u3001\u30a2\u30d5\u30ea\u30d9\u30eb\u30bb\u30d7\u30c8\u3068\u6bd4\u8f03\u3057\u3066\u826f\u597d\u306a\u6d6e\u816b\u6291\u5236\u3068\u6ce8\u5c04\u983b\u5ea6\u524a\u6e1b\u3092\u78ba\u8a8d\u3002<\/li>\n<\/ul>\n\n\n\n<p>&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8212;&#8211;<\/p>\n\n\n\n<h2 class=\"wp-block-heading\">6. \u8ab2\u984c\u3068\u5c55\u671b<\/h2>\n\n\n\n<ol class=\"wp-block-list\">\n<li><strong>\u5408\u4f75\u75c7\u306e\u7ba1\u7406:<\/strong> \u907a\u4f1d\u5b50\u6cbb\u7642\u306b\u4f34\u3046\u773c\u5185\u708e\u75c7\uff08IOI\uff09\u3084\u7db2\u819c\u840e\u7e2e\uff08CRA\uff09\u3078\u306e\u5bfe\u7b56\u304c\u4e0d\u53ef\u6b20\u3067\u3042\u308b\u3002<\/li>\n\n\n\n<li><strong>\u7d4c\u6e08\u7684\u8ad6\u70b9:<\/strong> \u30eb\u30af\u30b9\u30bf\u30fc\u30ca\u306b\u4ee3\u8868\u3055\u308c\u308b\u8d85\u9ad8\u984d\u88fd\u5264\u306e\u4fdd\u967a\u511f\u9084\u67a0\u7d44\u307f\u306f\u3001\u4eca\u5f8c\u306e\u518d\u751f\u533b\u7642\u666e\u53ca\u306b\u304a\u3051\u308b\u5927\u304d\u306a\u8ad6\u70b9\u3068\u306a\u308b\u3002<\/li>\n\n\n\n<li><strong>\u6280\u8853\u7684\u9032\u5c55:<\/strong> iPS\u7d30\u80de\u7531\u6765\u306e3\u6b21\u5143\u7db2\u819c\u7d44\u7e54\uff08\u30b7\u30fc\u30c8\uff09\u79fb\u690d\u306a\u3069\u3001\u3088\u308a\u9ad8\u5ea6\u306a\u6a5f\u80fd\u518d\u69cb\u7bc9\u3092\u76ee\u6307\u3059\u7814\u7a76\u304c\u9032\u5c55\u3057\u3066\u3044\u308b\u3002<\/li>\n<\/ol>\n\n\n\n<p>\u773c\u79d1\u9818\u57df\u306f\u3001\u4f4e\u4fb5\u8972\u306a\u624b\u8853\u624b\u6280\u3068\u753b\u50cf\u8a3a\u65ad\u6280\u8853\uff08OCT\u7b49\uff09\u306e\u9032\u6b69\u306b\u3088\u308a\u3001\u518d\u751f\u533b\u7642\u306e\u52b9\u679c\u3092\u5ba2\u89b3\u7684\u306b\u8a55\u4fa1\u3057\u3084\u3059\u3044\u3002\u4eca\u5f8c\u3001\u521d\u671f\u6bb5\u968e\uff08Early-stage\uff09\u306e\u81e8\u5e8a\u8a66\u9a13\u304b\u3089\u3001\u5927\u898f\u6a21\u306aPhase 3\u8a66\u9a13\u3078\u3068\u591a\u304f\u306e\u30d7\u30ed\u30b0\u30e9\u30e0\u304c\u79fb\u884c\u3057\u3066\u3044\u304f\u3053\u3068\u304c\u4e88\u6e2c\u3055\u308c\u308b\u3002<\/p>\n","protected":false},"excerpt":{"rendered":"\u773c\u79d1\u9818\u57df\u306b\u304a\u3051\u308b\u518d\u751f\u533b\u7642\u3068\u907a\u4f1d\u5b50\u6cbb\u7642\uff1a\u6700\u65b0\u52d5\u5411\u3068\u81e8\u5e8a\u7684\u8003\u5bdf \u30a8\u30b0\u30bc\u30af\u30c6\u30a3\u30d6\u30fb\u30b5\u30de\u30ea\u30fc \u773c\u79d1\u9818\u57df\u306f\u3001\u518d\u751f\u533b\u7642\u304a\u3088\u3073\u907a\u4f1d\u5b50\u6cbb\u7642\u306e\u793e\u4f1a\u5b9f\u88c5\u306b\u304a\u3044\u3066\u4e16\u754c\u3092\u30ea\u30fc\u30c9\u3059\u308b\u5206\u91ce\u3067\u3042\u308b\u3002\u773c\u7403\u306f\u300c\u514d\u75ab\u7279\u6a29\uff08Immune Privilege\uff09 [&hellip;]","protected":false},"author":1,"featured_media":509,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"_jetpack_memberships_contains_paid_content":false,"footnotes":""},"categories":[16,32,23,33],"tags":[],"class_list":["post-507","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-textbook","category-32","category-23","category-33"],"jetpack_featured_media_url":"https:\/\/rmnw.jp\/teams\/wp-content\/uploads\/2026\/05\/\u518d\u751f\u533b\u7642\u30cd\u30c3\u30c8\u30ef\u30fc\u30af\u30e6\u30fc\u30b6\u30fc-69f978a234705.png","jetpack_sharing_enabled":true,"_links":{"self":[{"href":"https:\/\/rmnw.jp\/teams\/index.php?rest_route=\/wp\/v2\/posts\/507","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/rmnw.jp\/teams\/index.php?rest_route=\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/rmnw.jp\/teams\/index.php?rest_route=\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/rmnw.jp\/teams\/index.php?rest_route=\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/rmnw.jp\/teams\/index.php?rest_route=%2Fwp%2Fv2%2Fcomments&post=507"}],"version-history":[{"count":1,"href":"https:\/\/rmnw.jp\/teams\/index.php?rest_route=\/wp\/v2\/posts\/507\/revisions"}],"predecessor-version":[{"id":510,"href":"https:\/\/rmnw.jp\/teams\/index.php?rest_route=\/wp\/v2\/posts\/507\/revisions\/510"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/rmnw.jp\/teams\/index.php?rest_route=\/wp\/v2\/media\/509"}],"wp:attachment":[{"href":"https:\/\/rmnw.jp\/teams\/index.php?rest_route=%2Fwp%2Fv2%2Fmedia&parent=507"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/rmnw.jp\/teams\/index.php?rest_route=%2Fwp%2Fv2%2Fcategories&post=507"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/rmnw.jp\/teams\/index.php?rest_route=%2Fwp%2Fv2%2Ftags&post=507"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}